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FOR FAMILIES LIVING WITH DUCHENNE MUSCULAR DYSTROPHY (DMD)

TOGETHER, LET’S MAKE IT HAPPEN

Spend more time enjoying the moments that matter and less time dealing with treatment access. When you enroll in PTC Cares, you’ll be connected with a dedicated Case Manager who will provide the expertise you need to help make the process of getting treatment easier on you. 

Two young boys standing with older sister and mother

Julian, individual living
with DMD, and family.

Two young boys standing with older sister and mother

See how we can help

This short video shows how your dedicated Case Manager will work with your insurance company and your healthcare provider to help you get started on treatment and set you up for long-term success.

Play video: What is PTC Cares?

Find a Case Manager

Connect with a Case Manager by entering your prescriber’s ZIP code. Then, call us at the number below. You may also complete one of the following patient consent forms:

  • Duchenne Muscular Dystrophy – Patient Consent Form
Help icon

We’re always ready to help!

1‑844‑4PTC‑CARES (1‑844‑478‑2227)

M – F, 8 AM – 6 PM ET

Financial assistance

We’re always working to support your access to treatment. Insurance benefits can vary widely and as a result, sometimes medications can be costly. That’s why we explore every available option to help minimize the cost to you. After your insurance evaluation is complete, we’ll call to go over any PTC financial assistance programs that may be available to your family, if eligible.

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The Copay Assistance Program*† can help qualified families who have commercial insurance get help covering out-of-pocket costs associated with treatment.

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The Bridge Program* can provide patients who are actively enrolled in PTC Cares a temporary supply of PTC medication free of charge while they are waiting for verification of insurance coverage.

If you need additional financial support, we’ll do our best to connect you to other charitable patient foundations that may be able to help.

  • * Low to no out-of-pocket costs for most patients who qualify.
  • †Not valid for prescriptions eligible to be reimbursed, in whole or in part, by Medicaid or Medicare (including Medicare Part D), or where prohibited by law.

Specialty pharmacy

When it comes to medication, we’re determined to deliver. Like many other therapies for rare diseases, medications from PTC Therapeutics are distributed through specialty pharmacies—pharmacies that are specially trained to handle them and can deliver them directly to your door. Specialty pharmacies can provide services, information, and support that regular pharmacies don’t offer. We’ll work closely with your specialty pharmacy throughout your treatment to coordinate the delivery of your medication.

Together, your specialty pharmacy and Case Manager will:

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Help you schedule deliveries to make sure your medication is delivered where and when you need it.

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Provide refill reminders to let you know when your refills are due.

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You will also receive a call from the specialty pharmacy each month to schedule your shipment. It’s very important to answer these calls, because your medication can’t be shipped without your confirmation and may not arrive on time if you miss a call.

We’ll always be available to answer any questions you may have about working with your specialty pharmacy. We’re just a phone call away. Call us at
1‑844‑4PTC‑CARES (1‑844‑478‑2227), M – F, 8 AM – 6 PM ET. We’re ready to help in any way we can.

Beyond treatment support

Get the personal attention you deserve. We know that families receiving treatment for DMD need more than just medicine. That’s why we’re committed to connecting you to support that goes beyond treatment support. Together, with our Patient Engagement partners, PTC can help connect you with the right information when you need it.

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Practical support: Not sure where to start when looking for a DMD specialist in your area? Need a contractor who knows how to modify your home for better accessibility? Our Patient Engagement team can connect you to the DMD community within your region so they can help you find the information and resources you need.

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Emotional support: Looking to connect with other families living with DMD? Want to discuss the details of a DMD-related decision your family needs to make? Whatever the issue, your dedicated Case Manager can connect you to a network of support, including our Patient Engagement team, or patient advocacy groups. We’re just a phone call away and ready to listen. Just call us at 1‑844‑4PTC‑CARES (1‑844‑478‑2227), M – F, 8 AM – 6 PM ET—even if you just want to talk when you’re having a particularly hard day.

Caregiver stories

Hear from other caregivers who understand your journey. Learn how other parents have managed challenges and achieved successes. Listen to what they have to say to help you gain insight into decisions you may need to make for your family. You can hear stories in English or Spanish, according to your preferences.

Play video: Challenging Expectations
View Transcript

Jessica Rothe, a mom, debunks misperceptions about the limitations for boys with a rare disease.

View Transcript

Sima Perez talks about her son and overcoming some of the hurdles that parents may face when it comes to school.

View Transcript

Sima Perez, a mom and caregiver, talks about the importance of self-care and support for caregivers.

Patient advocacy groups

Connect with the community. Patient advocacy groups provide education, resources, and support to members of the DMD community. The groups listed below are just a few of many organizations. Talk to your Case Manager for more information about advocacy groups and how they might be able to help your family.

CureDuchenne logo
CureDuchenne is a nonprofit organization that supports Duchenne-related research and features events, workshops, webinars, and more on its website.

You are now leaving the PTC Cares™ website and entering a website operated by an independent third party. The links to third-party websites contained on PTC Cares are provided solely for your convenience. PTC Therapeutics does not control the opinions, claims, or comments contained on any third-party website linked to PTC Cares, and your activities at those websites will be governed by the policies and practices of those third parties.

Continue

PTC does not warrant, whether expressed or implied, that the list of centers is accurate or complete. PTC does not recommend or endorse any center, hospital, or healthcare professional included above for any purpose, nor is the list to verify a center’s, hospital’s, or specific healthcare professional’s credentials or qualifications. It is your responsibility to select a center, hospital, and/or healthcare professional appropriate for your needs and you assume full responsibility for your interactions with any center, hospital, or healthcare professional you contact through the center list. PTC is not responsible for the medical care or advice given by any center, hospital, or healthcare professional you choose to contact.

Trademarks, registered or otherwise, are the property of their respective owner(s).

Parent Project Muscular Dystrophy Logo
Parent Project Muscular Dystrophy centers provide comprehensive care specifically for people living with Duchenne muscular dystrophy.

You are now leaving the PTC Cares™ website and entering a website operated by an independent third party. The links to third-party websites contained on PTC Cares are provided solely for your convenience. PTC Therapeutics does not control the opinions, claims, or comments contained on any third-party website linked to PTC Cares, and your activities at those websites will be governed by the policies and practices of those third parties.

Continue

PTC does not warrant, whether expressed or implied, that the list of centers is accurate or complete. PTC does not recommend or endorse any center, hospital, or healthcare professional included above for any purpose, nor is the list to verify a center’s, hospital’s, or specific healthcare professional’s credentials or qualifications. It is your responsibility to select a center, hospital, and/or healthcare professional appropriate for your needs and you assume full responsibility for your interactions with any center, hospital, or healthcare professional you contact through the center list. PTC is not responsible for the medical care or advice given by any center, hospital, or healthcare professional you choose to contact.

Trademarks, registered or otherwise, are the property of their respective owner(s).

Muscular Dystrophy Association Logo
Muscular Dystrophy Association (MDA) has more than 150 care clinics in the United States and Puerto Rico, each home to a full team of healthcare professionals.

You are now leaving the PTC Cares™ website and entering a website operated by an independent third party. The links to third-party websites contained on PTC Cares are provided solely for your convenience. PTC Therapeutics does not control the opinions, claims, or comments contained on any third-party website linked to PTC Cares, and your activities at those websites will be governed by the policies and practices of those third parties.

Continue

PTC does not warrant, whether expressed or implied, that the list of centers is accurate or complete. PTC does not recommend or endorse any center, hospital, or healthcare professional included above for any purpose, nor is the list to verify a center’s, hospital’s, or specific healthcare professional’s credentials or qualifications. It is your responsibility to select a center, hospital, and/or healthcare professional appropriate for your needs and you assume full responsibility for your interactions with any center, hospital, or healthcare professional you contact through the center list. PTC is not responsible for the medical care or advice given by any center, hospital, or healthcare professional you choose to contact.

Trademarks, registered or otherwise, are the property of their respective owner(s).

Jett Foundation Logo
Jett Foundation partners with individuals and families with Duchenne muscular dystrophy and other neuromuscular diseases through empowering educational programming, transformational direct service experiences, and by accelerating development of life‑changing treatments.

You are now leaving the PTC Cares™ website and entering a website operated by an independent third party. The links to third-party websites contained on PTC Cares are provided solely for your convenience. PTC Therapeutics does not control the opinions, claims, or comments contained on any third-party website linked to PTC Cares, and your activities at those websites will be governed by the policies and practices of those third parties.

Continue

PTC does not warrant, whether expressed or implied, that the list of centers is accurate or complete. PTC does not recommend or endorse any center, hospital, or healthcare professional included above for any purpose, nor is the list to verify a center’s, hospital’s, or specific healthcare professional’s credentials or qualifications. It is your responsibility to select a center, hospital, and/or healthcare professional appropriate for your needs and you assume full responsibility for your interactions with any center, hospital, or healthcare professional you contact through the center list. PTC is not responsible for the medical care or advice given by any center, hospital, or healthcare professional you choose to contact.

Trademarks, registered or otherwise, are the property of their respective owner(s).

The Assistance Fund Logo
The Assistance Fund helps patients with high medical out-of-pocket costs. For eligible patients, the fund provides financial assistance to cover costs not paid for by insurance.

You are now leaving the PTC Cares™ website and entering a website operated by an independent third party. The links to third-party websites contained on PTC Cares are provided solely for your convenience. PTC Therapeutics does not control the opinions, claims, or comments contained on any third-party website linked to PTC Cares, and your activities at those websites will be governed by the policies and practices of those third parties.

Continue

PTC does not warrant, whether expressed or implied, that the list of centers is accurate or complete. PTC does not recommend or endorse any center, hospital, or healthcare professional included above for any purpose, nor is the list to verify a center’s, hospital’s, or specific healthcare professional’s credentials or qualifications. It is your responsibility to select a center, hospital, and/or healthcare professional appropriate for your needs and you assume full responsibility for your interactions with any center, hospital, or healthcare professional you contact through the center list. PTC is not responsible for the medical care or advice given by any center, hospital, or healthcare professional you choose to contact.

Trademarks, registered or otherwise, are the property of their respective owner(s).

Resources

Prescription Start Form

Treatment begins with the Prescription Start Form that you and your healthcare provider fill out and your provider faxes to us.

Prescription Start Form
Prescription Start Form
Download
Prescribing Information and Medication Guide
Prescribing Information and Medication Guide
Download
Clinic Visit Readiness Sheet

Clinic Visit Readiness Sheet

Gather and record important information or questions for your healthcare provider so you can make the most of your next visit.

Download
Insurance Glossary

Insurance Glossary

A glossary of commonly used terms that can help prepare you for important insurance-related conversations.

Download
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We are always ready to help

1-844-4PTC-CARES (1-844-478-2227)
M – F, 8 AM – 6 PM ET

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Frequently asked questions

Get answers to commonly asked questions about insurance, affordability, or getting medication.

View FAQs
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About us

Find out more about who we are and how we help families living with rare diseases.

See how we help
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© 2025 PTC Therapeutics, Inc. All Rights Reserved. US-CORP-0237  07/25

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