Rylae, individual living with AADC deficiency.
Find a Case Manager
Connect with a Case Manager by entering your prescriber’s ZIP code. Then, call us at the number below or complete the AADC deficiency Patient Consent Form to get connected with your dedicated Case Manager.
Financial assistance
Beyond treatment support
Patient advocacy groups
Connect with the community. Patient advocacy groups provide education, resources, and support to members of the AADC community. The groups listed below are just a few of many organizations that offer support for people living with rare diseases, including AADC deficiency. Talk to your Case Manager for more information about advocacy groups and how they might be able to help your family.
You are now leaving the PTC Cares™ website and entering a website operated by an independent third party. The links to third-party websites contained on PTC Cares are provided solely for your convenience. PTC Therapeutics does not control the opinions, claims, or comments contained on any third-party website linked to PTC Cares, and your activities at those websites will be governed by the policies and practices of those third parties.
PTC does not warrant, whether expressed or implied, that the list of centers is accurate or complete. PTC does not recommend or endorse any center, hospital, or healthcare professional included above for any purpose, nor is the list to verify a center’s, hospital’s, or specific healthcare professional’s credentials or qualifications. It is your responsibility to select a center, hospital, and/or healthcare professional appropriate for your needs and you assume full responsibility for your interactions with any center, hospital, or healthcare professional you contact through the center list. PTC is not responsible for the medical care or advice given by any center, hospital, or healthcare professional you choose to contact.
Trademarks, registered or otherwise, are the property of their respective owner(s).
You are now leaving the PTC Cares™ website and entering a website operated by an independent third party. The links to third-party websites contained on PTC Cares are provided solely for your convenience. PTC Therapeutics does not control the opinions, claims, or comments contained on any third-party website linked to PTC Cares, and your activities at those websites will be governed by the policies and practices of those third parties.
PTC does not warrant, whether expressed or implied, that the list of centers is accurate or complete. PTC does not recommend or endorse any center, hospital, or healthcare professional included above for any purpose, nor is the list to verify a center’s, hospital’s, or specific healthcare professional’s credentials or qualifications. It is your responsibility to select a center, hospital, and/or healthcare professional appropriate for your needs and you assume full responsibility for your interactions with any center, hospital, or healthcare professional you contact through the center list. PTC is not responsible for the medical care or advice given by any center, hospital, or healthcare professional you choose to contact.
Trademarks, registered or otherwise, are the property of their respective owner(s).
You are now leaving the PTC Cares™ website and entering a website operated by an independent third party. The links to third-party websites contained on PTC Cares are provided solely for your convenience. PTC Therapeutics does not control the opinions, claims, or comments contained on any third-party website linked to PTC Cares, and your activities at those websites will be governed by the policies and practices of those third parties.
PTC does not warrant, whether expressed or implied, that the list of centers is accurate or complete. PTC does not recommend or endorse any center, hospital, or healthcare professional included above for any purpose, nor is the list to verify a center’s, hospital’s, or specific healthcare professional’s credentials or qualifications. It is your responsibility to select a center, hospital, and/or healthcare professional appropriate for your needs and you assume full responsibility for your interactions with any center, hospital, or healthcare professional you contact through the center list. PTC is not responsible for the medical care or advice given by any center, hospital, or healthcare professional you choose to contact.
Trademarks, registered or otherwise, are the property of their respective owner(s).
Resources
Insurance Glossary
A glossary of commonly used terms that can help prepare you for important insurance-related conversations.
We are always ready to help
1-844-4PTC-CARES (1-844-478-2227)
M – F, 8 AM – 6 PM ET
Frequently asked questions
Get answers to commonly asked questions about insurance, affordability, or getting medication.
About us
Find out more about who we are and how we help families living with rare diseases.